No abstract available
Keywords:
Drug discovery; Gene therapy; Neurodegeneration.
MeSH terms
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Disease Progression
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Female
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Genetic Therapy / adverse effects*
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Hope
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Humans
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Huntingtin Protein / deficiency
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Huntingtin Protein / genetics
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Huntingtin Protein / metabolism
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Huntington Disease / genetics*
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Huntington Disease / therapy*
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Mutant Proteins / genetics
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Mutant Proteins / metabolism
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Oligonucleotides / administration & dosage
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Oligonucleotides / adverse effects*
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Oligonucleotides / therapeutic use*
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Oligonucleotides, Antisense / administration & dosage
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Oligonucleotides, Antisense / adverse effects*
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Oligonucleotides, Antisense / therapeutic use*
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Optimism
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Treatment Failure
Substances
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HTT protein, human
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Huntingtin Protein
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Mutant Proteins
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Oligonucleotides
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Oligonucleotides, Antisense
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tominersen