Impaired intrinsic immunity to HSV-1 in human iPSC-derived TLR3-deficient CNS cells

Nature. 2012 Nov 29;491(7426):769-73. doi: 10.1038/nature11583. Epub 2012 Oct 28.

Abstract

In the course of primary infection with herpes simplex virus 1 (HSV-1), children with inborn errors of toll-like receptor 3 (TLR3) immunity are prone to HSV-1 encephalitis (HSE). We tested the hypothesis that the pathogenesis of HSE involves non-haematopoietic CNS-resident cells. We derived induced pluripotent stem cells (iPSCs) from the dermal fibroblasts of TLR3- and UNC-93B-deficient patients and from controls. These iPSCs were differentiated into highly purified populations of neural stem cells (NSCs), neurons, astrocytes and oligodendrocytes. The induction of interferon-β (IFN-β) and/or IFN-λ1 in response to stimulation by the dsRNA analogue polyinosinic:polycytidylic acid (poly(I:C)) was dependent on TLR3 and UNC-93B in all cells tested. However, the induction of IFN-β and IFN-λ1 in response to HSV-1 infection was impaired selectively in UNC-93B-deficient neurons and oligodendrocytes. These cells were also much more susceptible to HSV-1 infection than control cells, whereas UNC-93B-deficient NSCs and astrocytes were not. TLR3-deficient neurons were also found to be susceptible to HSV-1 infection. The rescue of UNC-93B- and TLR3-deficient cells with the corresponding wild-type allele showed that the genetic defect was the cause of the poly(I:C) and HSV-1 phenotypes. The viral infection phenotype was rescued further by treatment with exogenous IFN-α or IFN-β ( IFN-α/β) but not IFN-λ1. Thus, impaired TLR3- and UNC-93B-dependent IFN-α/β intrinsic immunity to HSV-1 in the CNS, in neurons and oligodendrocytes in particular, may underlie the pathogenesis of HSE in children with TLR3-pathway deficiencies.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Astrocytes / immunology
  • Astrocytes / virology
  • Biomarkers
  • Cell Differentiation
  • Cell Lineage
  • Cell Separation
  • Cells, Cultured
  • Central Nervous System / cytology
  • Central Nervous System / immunology
  • Central Nervous System / pathology*
  • Central Nervous System / virology
  • Child
  • Disease Susceptibility
  • Encephalitis, Herpes Simplex / immunology
  • Encephalitis, Herpes Simplex / metabolism
  • Encephalitis, Herpes Simplex / pathology
  • Encephalitis, Herpes Simplex / virology
  • Herpesvirus 1, Human / immunology*
  • Herpesvirus 1, Human / pathogenicity
  • Humans
  • Immunity, Innate
  • Induced Pluripotent Stem Cells / cytology*
  • Induced Pluripotent Stem Cells / virology
  • Interferons / immunology
  • Membrane Transport Proteins / deficiency
  • Membrane Transport Proteins / genetics
  • Neural Stem Cells / immunology
  • Neural Stem Cells / virology
  • Neurons / immunology
  • Neurons / pathology
  • Neurons / virology
  • Oligodendroglia / immunology
  • Oligodendroglia / pathology
  • Oligodendroglia / virology
  • Toll-Like Receptor 3 / deficiency*
  • Toll-Like Receptor 3 / genetics

Substances

  • Biomarkers
  • Membrane Transport Proteins
  • TLR3 protein, human
  • Toll-Like Receptor 3
  • UNC93B1 protein, human
  • Interferons

Associated data

  • GEO/GSE40593