No abstract available
Keywords:
Cystic Fibrosis.
MeSH terms
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Aminophenols / therapeutic use*
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Aminopyridines / therapeutic use*
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Benzodioxoles / therapeutic use*
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Cystic Fibrosis / drug therapy*
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Cystic Fibrosis / genetics
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Cystic Fibrosis Transmembrane Conductance Regulator / genetics*
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Drug Combinations
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Gene Deletion*
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Homozygote
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Humans
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Molecular Targeted Therapy / methods
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Quinolones / therapeutic use*
Substances
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Aminophenols
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Aminopyridines
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Benzodioxoles
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CFTR protein, human
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Drug Combinations
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Quinolones
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Cystic Fibrosis Transmembrane Conductance Regulator
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ivacaftor
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lumacaftor