Novel pathogenic COX20 variants causing dysarthria, ataxia, and sensory neuropathy

Ann Clin Transl Neurol. 2018 Nov 9;6(1):154-160. doi: 10.1002/acn3.661. eCollection 2019 Jan.

Abstract

COX20/FAM36A encodes a mitochondrial complex IV assembly factor important for COX2 activation. Only one homozygous COX20 missense mutation has been previously described in two separate consanguineous families. We report four subjects with features that include childhood hypotonia, areflexia, ataxia, dysarthria, dystonia, and sensory neuropathy. Exome sequencing in all four subjects identified the same novel COX20 variants. One variant affected the splice donor site of intron-one (c.41A>G), while the other variant (c.157+3G>C) affected the splice donor site of intron-two. cDNA and protein analysis indicated that no full-length cDNA or protein was generated. These subjects expand the phenotype associated with COX20 deficiency.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, N.I.H., Intramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Ataxia / genetics*
  • Child
  • Dysarthria / genetics*
  • Electron Transport Complex IV / genetics*
  • Female
  • Hereditary Sensory and Autonomic Neuropathies / genetics*
  • Humans
  • Male
  • Pedigree
  • Phenotype

Substances

  • COX20 protein, human
  • Electron Transport Complex IV