Revised Recommendations for the Treatment of Infants Diagnosed with Spinal Muscular Atrophy Via Newborn Screening Who Have 4 Copies of SMN2

Affiliations

• ¹ Cure SMA, Elk Grove Village, IL, USA.
• ² Stanford University, Stanford, CA, USA.
• ³ Washington University School of Medicine, St. Louis, MO, USA.
• ⁴ Department of Neurology, Boston Children's Hospital, Boston, MA, USA.
• ⁵ Nemours Children's Hospital, University of Central Florida College of Medicine, Orlando, FL, USA.
• ⁶ Miller School of Medicine, University of Miami, Miami, FL, USA.
• ⁷ Genzyme Corporation, a Sanofi Company, Framingham, MA, USA.
• ⁸ Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, IL, USA.
• ⁹ Department of Molecular Pathology, Ohio State Wexner Medical Center, Columbus, OH, USA.
• ¹⁰ University of California Los Angeles, Los Angeles, CA, USA.
• ¹¹ Departments of Neurology and Pediatrics, Johns Hopkins University, Baltimore, MD, USA.
• ¹² Generation Bio, Cambridge, MA, USA.