Eradication of metastatic mouse cancers resistant to immune checkpoint blockade by suppression of myeloid-derived cells

Proc Natl Acad Sci U S A. 2014 Aug 12;111(32):11774-9. doi: 10.1073/pnas.1410626111. Epub 2014 Jul 28.

Abstract

Impressive responses have been observed in patients treated with checkpoint inhibitory anti-programmed cell death-1 (PD-1) or anti-cytotoxic T-lymphocyte-associated antigen-4 (CTLA-4) antibodies. However, immunotherapy against poorly immunogenic cancers remains a challenge. Here we report that treatment with both anti-PD-1 and anti-CTLA-4 antibodies was unable to eradicate large, modestly immunogenic CT26 tumors or metastatic 4T1 tumors. Cotreatment with epigenetic-modulating drugs and checkpoint inhibitors markedly improved treatment outcomes, curing more than 80% of the tumor-bearing mice. Functional studies revealed that the primary targets of the epigenetic modulators were myeloid-derived suppressor cells (MDSCs). A PI3K inhibitor that reduced circulating MDSCs also eradicated 4T1 tumors in 80% of the mice when combined with immune checkpoint inhibitors. Thus, cancers resistant to immune checkpoint blockade can be cured by eliminating MDSCs.

Keywords: 5-azacytidine; HDAC; entinostat; exome; methyltransferase.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antibodies, Monoclonal / administration & dosage
  • Azacitidine / administration & dosage
  • Benzamides / administration & dosage
  • CTLA-4 Antigen / antagonists & inhibitors
  • CTLA-4 Antigen / immunology
  • Cell Line, Tumor
  • Colorectal Neoplasms / immunology
  • Colorectal Neoplasms / secondary
  • Colorectal Neoplasms / therapy
  • Combined Modality Therapy
  • Epigenesis, Genetic / drug effects
  • Female
  • Histone Deacetylase Inhibitors / administration & dosage
  • Humans
  • Immunotherapy / methods*
  • Mammary Neoplasms, Experimental / immunology
  • Mammary Neoplasms, Experimental / secondary
  • Mammary Neoplasms, Experimental / therapy
  • Mice
  • Mice, Inbred BALB C
  • Myeloid Cells / drug effects
  • Myeloid Cells / immunology*
  • Neoplasm Metastasis / genetics
  • Neoplasm Metastasis / immunology*
  • Neoplasm Metastasis / therapy*
  • Phosphoinositide-3 Kinase Inhibitors
  • Programmed Cell Death 1 Receptor / antagonists & inhibitors
  • Programmed Cell Death 1 Receptor / immunology
  • Pyridines / administration & dosage

Substances

  • Antibodies, Monoclonal
  • Benzamides
  • CTLA-4 Antigen
  • Histone Deacetylase Inhibitors
  • Pdcd1 protein, mouse
  • Phosphoinositide-3 Kinase Inhibitors
  • Programmed Cell Death 1 Receptor
  • Pyridines
  • entinostat
  • Azacitidine